Study of Circular RNA Treatment in Patients With Radiation Induced Xerostomia-1

Purpose

This is a first-in-human clinical study to evaluate the safety, tolerability and efficacy of RXRG001 administered in the ducts of the parotid glands in adult patients with radiation-induced xerostomia (dry mouth) and hyposalivation (reduced saliva production). In Part 1 of the study (open-label, single-arm), patients will receive unilateral administrations of RXRG001 in 3 single ascending dose cohorts and in 3 multiple ascending dose cohorts. Part 2 of the study has a randomized, double-blind, placebo-controlled design. Patients will receive bilateral administrations of RXRG001 in 3 multiple ascending dose cohorts.

Condition

  • Radiation-Induced Xerostomia and Hyposalivation

Eligibility

Eligible Ages
Over 18 Years
Eligible Sex
All
Accepts Healthy Volunteers
No

Inclusion Criteria

* 1. At least 18 years of age 2. Free from recurrence of your cancer and never have had another form of cancer for at least 2 years 3. Suffering from xerostomia and/or hyposalivation and have xerostomia symptoms which were not resolved after treatment for at least 3 months 4. Both parotid glands on imaging examination

Exclusion Criteria

* 1. Any active infection 2. Heart failure, reduced kidney function or uncontrolled diabetes (Hemoglobin A1c >=8%) 3. History of autoimmune diseases known to potentially affect the salivary glands 4. Any malignancy, other than head and neck cancer within the past 3 years except for certain skin and cervical cancers 5. Active smoker or use tobacco products or have a history of substance or alcohol abuse - Other criteria apply

Study Design

Phase
Phase 1/Phase 2
Study Type
Interventional
Allocation
Randomized
Intervention Model
Parallel Assignment
Intervention Model Description
Part 1 (Phase 1): single-arm, open-label Part 2 (Phase 2): randomized, double-blind, placebo-controlled, parallel-group
Primary Purpose
Treatment
Masking
Double (Participant, Investigator)
Masking Description
Part 1 (Phase 1): single-arm open-label Part 2 (Phase2): randomized, double-blind, placebo-controlled, parallel-group

Arm Groups

ArmDescriptionAssigned Intervention
Experimental
RXRG001 Part 1
Open-label, single arm with 6 subsequent dose cohorts (3 single dose and 3 multiple dose cohorts) of RXRG001 administered intraductally in the salivary gland (unilateral)
  • Biological: RXRG001
    Circular ribonucleic acid encoding human aquaporin 1 encapsulated in a lipid nanoparticle
Experimental
RXRG001 Part 2
Randomized double-blind with 3 subsequent multiple dose cohorts. RXRG001 is administered intraductally in the salivary gland (bilateral)
  • Biological: RXRG001
    Circular ribonucleic acid encoding human aquaporin 1 encapsulated in a lipid nanoparticle
Placebo Comparator
Placebo Part 2
Randomized double-blind with 3 subsequent multiple dose cohorts. Placebo is administered intraductally in the salivary gland (bilateral)
  • Biological: Placebo
    Placebo (saline)

Recruiting Locations

University of Iowa Hospitals and Clinics
Iowa City, Iowa 52242
Contact:
Principal Investigator

John Hopkins University, Sidney Kimmel Comprehensive Cancer Center
Baltimore, Maryland 21287
Contact:
Principal Investigator

NYU Langone Medical Center
New York, New York 10016-6402
Contact:
Principal Investigator

Penn Medicine - Otorhinolaryngology - Head and Neck Surgery Perelman
Philadelphia, Pennsylvania 19104
Contact:
Principal Investigator

More Details

NCT ID
NCT06714253
Status
Recruiting
Sponsor
RiboX Therapeutics Ltd.

Study Contact

RiboX Therapeutics Ltd.
609 212 2832
RiboX-SPRINX1-RX-RIX-CS101-Study-Mailbox@ribox-tx.com